ema_orphan_designations

Pack: ema-medicines · Connect: https://pipeworx.io/mcp (see Connect below for a single-pack URL)

No MCP client? Call it directly: GET https://gateway.pipeworx.io/v1/tools/ema_orphan_designations for the schema, then POST the same URL with its arguments for the data.

European Medicines Agency orphan medicinal product designations — active substances designated by the EU as treatments for rare diseases, which carry incentives like protocol assistance and market exclusivity. Returns the active substance, medicine name (once assigned), intended therapeutic use, EU designation number, designation status (Positive, Withdrawn, Expired, Negative) and dates. Catalyst-relevant for biotech: a positive designation often precedes a clinical or regulatory catalyst by months to years. Answers “what orphan designations has the EMA granted for rare disease X”, “is drug X an EU-designated orphan medicine”, “recent EU orphan designations”.

Parameters

Example call

Arguments

{
  "status": "Positive",
  "since": "2026-01"
}

curl

curl -X POST https://gateway.pipeworx.io/ema-medicines/mcp \
  -H 'Content-Type: application/json' \
  -d '{"jsonrpc":"2.0","id":1,"method":"tools/call","params":{"name":"ema_orphan_designations","arguments":{"status":"Positive","since":"2026-01"}}}'

TypeScript (@pipeworx/sdk)

import { Pipeworx } from '@pipeworx/sdk';
const pipeworx = new Pipeworx();

const result = await pipeworx.call('ema_orphan_designations', {
  "status": "Positive",
  "since": "2026-01"
});

More examples

{
  "query": "severe combined immunodeficiency",
  "limit": 5
}

Connect

Add this to your MCP client config — every tool in the catalog, including this one — or use one-click install buttons:

{
  "mcpServers": {
    "pipeworx": {
      "url": "https://pipeworx.io/mcp"
    }
  }
}

{
  "mcpServers": {
    "ema-medicines": {
      "url": "https://gateway.pipeworx.io/ema-medicines/mcp"
    }
  }
}

See Getting Started for client-specific install steps.